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Spinal muscular atrophy

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The global impact of brain disorders

The Brain Health Atlas infographic was developed to measure the global burden of brain disorders over time and geographies.

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How adult SMA patients improve access to care and treatment

Three letters – SMA – tell countless personal stories. Stories of resilience, as adults living with spinal muscular atrophy (SMA) navigate everyday life and overcome challenges to access care and treatment.

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What makes you, you: Seda's story

Seda lives with spinal muscular atrophy (SMA). She takes us through a day in her life, sharing how her advocacy work, hobbies and passions make her unique.

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Addressing urgent gaps in care for adults living with SMA

Adults make up more than half of those living with SMA yet many face significant obstacles in accessing the care and treatment they need

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Building a historic alliance to shape the future of SMA

How a unique alliance between the SMA Foundation, PTC Therapeutics and Roche changed the trajectory for SMA patients.

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Spinal Muscular Atrophy (SMA) screening for newborns in Europe

Early detection is important in many conditions, but it is particularly true in SMA as the loss of motor neurons that control muscles cannot be regenerated

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The continuing evolution of clinical trials

Nowadays, clinical trials are highly structured and regulated, ensuring the safety of the participants, but this hasn't always been the case.

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Bringing patient support to a rare disease

Learn how we are breaking down barriers that prevent patients from joining clinical trials for spinal muscular atrophy.

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Living life your way with SMA My Way

We have so much to learn from each other about tackling the everyday challenges of spinal muscular atrophy. Find out how we can through SMA My Way.

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The power of partnership

With a shared dedication to bring innovative treatments to SMA patients, the SMA Foundation, PTC Therapeutics and Roche show the power of collaboration.

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